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Dergiler / Aurum Journal of Health Sciences / 2019 / Cilt: 1 Sayı: 2

Rare Disease and Orphan Drug Situations in Turkey and around the World

Buket Aksu(ALTINBAŞ ÜNİVERSİTESİ)0000-0001-7555-0603
Sayfa
95–109
Yayın Tarihi
2019-03-31
DOI
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⚡ TL;DR(1 Cümlede Hızlı Çıkarım)

This group of diseases is a highly

📌 3 Maddede Bu Makale

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Amaç & Hipotez:Abstract: Diseases with a prevalence less than 1/2000 are defined as “Rare Diseases”.
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Temel Bulgular & Veri:Abstract: Diseases with a prevalence less than 1/2000 are defined as “Rare Diseases”.
💡
Sonuç & Katkı:This group of diseases is a highly
🔬Tür:Diğer
📍Kapsam:2000 Verileri
⚙️Değişkenler:Rare · disease · orphan

Abstract

Abstract: Diseases with a prevalence less than 1/2000 are defined as “Rare Diseases”. This group of diseases is a highly

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Bu Makaleye Atıf Yap

Aksu, B. (2019). Rare Disease and Orphan Drug Situations in Turkey and around the World. Aurum Journal of Health Sciences, Cilt: 1 Sayı: 2, 95–109. https://ajindex.com/articles/1581154

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Kaynakça (23)

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  2. Akıcı, A., Ulupınar, S. (2015). The Role of Patient Care Personnel in Rational Drug Use, Social Security Institution Brochure, http://gss.sgk.gov.tr/aik/toplum/hastayardimci/doc/hastabakimaikbrosur.pdf (accessed May 2015).
  3. Balık, İ. (2014). Association of Research-Based Pharmaceutical Companies (AIFD) Rare Diseases and Orphan Medicine Symposium Orphan Drug Regulation Workshop Book, 13-14 September.
  4. Blankart, R.C., Stargardt, T., Schreyogg, J. (2011). Availability of and access to orphan drugs. Pharmacoeconomics, 29:63–82.
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  7. Denis, A., Mergaert, L., Fostier, C., Cleemput, I., Simoens, S. (2010). Issues surrounding orphan disease and orphan drug policies in Europe. Appl Health Econ Health Policy., 8, 343-50.
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  13. Gammie, T., Lu, C.Y., Babar, Z.D. (2015). Access to Orphan Drugs: A Comprehensive Review of Legislations, Regulations and Policies in 35 Countries. PlosOne., 10, 1-24.
  14. Hadjivasiliou, A. (2014). Orphan Drug Report 2014. Evaluate Pharma., 3-19
  15. Kesselheim, A.S., Myers, J.A., Avorn, J. (2011). Characteristics of clinical trials to support approval of orphan vs non-orphan drugs for cancer. JAMA., 305, 2320-2326.
  16. Orphanet’ Rare diseases in numbers: preliminary report from an ongoing bibliographic study initiated by Eurordis in partnership with Orphanet, https://www.orpha.net/actor/Orphanews/2005/doc/Rare_ Diseases_in_Numbers.pdf (accessed 10 December 2016)
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  19. Sosyal Güvenlik Kurumu Çalışanlarının Akılcı İlaç Kullanımındaki Etkin Rolü ve Farmakoekonomi. (2013). Book T.C. Social Security Institution, Publication No: 114
  20. Stolk, P., Willemen, M.J., Leufkens, H.G. (2006). Rare essentials: drugs for rare diseases as essential medicines. Bull World Health Organ., 84, 745-751.
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