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Yapay Zeka Hızlı Bakış & Çıkarımlar
AI Insight⚡ TL;DR(1 Cümlede Hızlı Çıkarım)
In this review, we summarize the ongoing clinical trials and molecular mechanisms of successful approaches to SMA treatment.
📌 3 Maddede Bu Makale
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Amaç & Hipotez:Proximal spinal muscular atrophy (SMA) is an inherited neurodegenerative disease with a heterogeneous clinical phenotype.
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Temel Bulgular & Veri:Although there is no cure for SMA, several strategies are currently being developed.
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Sonuç & Katkı:In this review, we summarize the ongoing clinical trials and molecular mechanisms of successful approaches to SMA treatment.
🔬Tür:Literatür & Derleme Çalışması
📍Kapsam:Genişletilmiş Akademik Örneklem
⚙️Değişkenler:Spinal muscular atrophy · therapeutic approaches · clinical trials
Abstract
Proximal spinal muscular atrophy (SMA) is an inherited neurodegenerative disease with a heterogeneous clinical phenotype. Although there is no cure for SMA, several strategies are currently being developed. In this review, we summarize the ongoing clinical trials and molecular mechanisms of successful approaches to SMA treatment.
Anahtar kelimeler
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Bu Makaleye Atıf Yap
BORA, G., YEŞBEK-KAYMAZ, A., BEKİRCAN-KURT, C. E., HALİLOĞLU, V. G., TOPALOĞLU, H. A., ERDEM-YURTER, H., ERDEM-ÖZDAMAR, S. (2018). Recent therapeutic developments in spinal muscular atrophy. Turkish Journal of Medical Sciences, Cilt: 48 - Sayı: 2, 203–211. https://ajindex.com/articles/112963